CHICAGO TRIBUNE: Duchenne muscular dystrophy drug could get OK for U.S. sales in 2016
The Chicago Tribune spoke to families and advocates seeking better treatment options for Duchenne muscular dystrophy as part of their coverage of Marathon Pharmaceuticals, a company working to earn U.S. approval for a Duchenne muscular dystrophy treatment.
A Northbrook company said it has won fast-track status for approval of a drug that could become the first in the United States to treat Duchenne muscular dystrophy, a fatal muscle disease found most often in boys...
U.S. Food and Drug Administration approval is eagerly awaited by people such as Ellen Wagner, whose son, Tim, was diagnosed at 2 with Duchenne. The McHenry mom began ordering deflazacort from the United Kingdom after the physician treating her son wrote a prescription. Its use in the U.S. is legal because there is no other approved treatment for Duchenne in the country.
